How your gift powers treatment

Your donation is not funding hope someday. It is funding life-changing treatment now—before Ivy’s developmental window closes. Every contribution funds a concrete step in n-Lorem’s proven pathway for creating personalized ASO treatments.

And the impact of your donation doesn’t stop there. n-Lorem’s success on Ivy’s case will benefit other patients will similar ultra-rare mutations, helping those who come after her get treated faster.

  • $250

    One hour of an n-Lorem scientist working on Ivy’s case

  • $1,000

    Small-scale synthesis of one candidate ASO in n-Lorem’s lab

  • $5,000

    Conduct an 8-week tolerability study of one candidate ASO in rats

  • $10,000

    Fund one of several critical safety tests on the final ASO

  • $60,000

    GMP Manufacturing of the final ASO

  • $150,000

    The last step: place the final ASO in sterile vials and seal them for transport to Ivy’s doctor

Donate now